Free

- 7 lessons
- 1 quizzes
- 10 week duration
Module 5
Target sites for Gene Therapy
| Disease | Target Cells |
|---|---|
| Infectious disease | Blood Progenitor cells, Antigen Presenting cells, Muscle cells |
| Cancer | Blood Progenitor cells, Antigen Presenting cells, Muscle cells, Tumor cells, Fibroblasts |
| Rheumatoid arthritis | Synovial lining cells |
| Inherited monogenic disease | Macrophages, Blood Progenitor Cells, Hepatocytes, Muscle cells |
| Cardiovascular Disease | Endothelial cells, Muscle cells |
