Systematic gene delivery

Gene Therapy Mechanism
A) Gene Augmentation Therapy
Gene Augmentation Therapy is used for the autosomal recessive disorder. In the case of GAT, the addition of alleles is applied to cure the inherited disease which is caused by the deficiency of a gene product.

B) Targeted killing of Specific Cells
The main approach of target killing leads to cancer gene therapies. It indulges the toxic compounds like prodrugs, which encodes to kill the transfected cells or transformed cells. C) Targeted Gene Mutation Correction TMGC is used to veracious a defective gene to restore its normal function which can be done at Gene level through homologous recombination mechanism by employing therapeutic ribozymes or RNA editing.